research

Fourteen year old Ali Zaidi has been part of a clinical trial of a new enzyme replacement drug for five years. Ali has Morquio Syndrome, a rare inherited metabolic disorder which causes an abnormal storage of large and complex sugar molecules within the cells of the body.

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How you can contribute after your treatment

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Until recently, no new drugs to treat children with cancer had been developed for several decades. This was because child cancer is rare and there was no incentive for big drug companies to spend money on producing new drugs specifically for cancer in children.

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